Listen to my newest Podcast. Click on the link where my updates are.
Updates From Trial of AveXis SMA1 Gene Therapy Trial Show Impressive Results in Most Infants
Avexis Announces Plan to Initiate Phase 1 Trial in SMA Type 2 Utilizing Intrathecal Delivery of AVXS-101
FDA Approves AveXis' Pivotal Trial of AVXS-101 For SMA Type 1
Study of Intrathecal Administration of AVXS-101 for SMA (STRONG)
Gene Replacement Therapy Clinical Trial for Patients With SMA Type 1 (STR1VE)
Biogen Unlikely To See Spinraza Rival In 2018 As AveXis Delayed
Local family with little one battling Spinal Muscular Atrophy says "miracle drug" is changing their daughters life
Clinical Trials Bring Hope to Kids with Spinal Muscular Atrophy
SMA Could Soon Be on Newborn Screening List in the U.S.
Moms push for newborn genetic screening so families avoid 'paralyzing grief'
Spinal Muscular Atrophy - Global market size will increase 2 folds by 2025
Young Man with Significant Disabilities Argues for Inclusion
This Man with Spinal Muscular Atrophy Has a Simple Way of Surviving Even Life's Biggest Challenges
Top trainee hopes unexpected discovery may help children with genetic disease
Two Good Options
Two New Ways to Treat A Deadly Disease: Spinal Muscular Atrophy
Gene therapy's new hope: A neuron-targeting virus is saving infant lives
Exosome-derived protein may serve as an effective biomarker for spinal muscular atropher
New hope for families affected by spinal muscular atrophy, with TGA approving drug
Nusinersen versus Sham Control in Infatile-Onset Spinal Muscular Atrophy
AveXis Announces New England Journal of Medical Publication of Phase 1 Data of AVXS-101 Gene Replacement Therapy in Spinal Muscular Atrophy Type 1
Gene replacement tx beneficial in spinal muscular atrophy
Experimental baby gene therapy offers solution to spinal muscular atrophy